Tag: Severe

Jaguar Health Announces Napo Therapeutics’ Submission of Orphan Drug Designation Application to the European Medicines Agency for Crofelemer for a Severe Congenital Diarrheal Disorder (CDD) Condition

Microvillus inclusion disease (MVID) is a life-threatening and rare autosomal recessive disease that affects newborns and children and leads to significant morbidity and mortality from severe secretory diarrhea SAN FRANCISCO, CA / ACCESSWIRE / May 25, 2022 / Jaguar Health (NASDAQ:JAGX) announced today that Napo Therapeutics, the Italian corporation established by the company in Italy in 2021 that focuses on …

BioMarin Resubmits Marketing Authorization Application (MAA) to European Medicines Agency for Valoctocogene Roxaparvovec to Treat Severe Hemophilia A

SAN RAFAEL, CALIFORNIA., June 28, 2021 / PRNewswire / – BioMarin Pharmaceutical Inc. (NASDAQ: BMRN) announced today that it has re-submitted a MAA from the European Medicines Agency (EMA) for its investigational therapy Valoctocogen roxaparvovec for adults with severe hemophilia A. submitted. in the May 2021, the EMA has granted the company’s accelerated assessment request. An accelerated assessment may shorten …

Toxicology Rounds: Ought to Fomepizole be Used to Deal with Extreme… : Emergency Drugs Information

Number: Fomepizole, paracetamol number The year 2020 is certainly one that we like to see in the rearview mirror. Much of the toxicology literature published in the past 12 months has looked at the adverse effects of unapproved and undetected treatments for COVID-19 such as chloroquine and hydroxychloroquine, but there have also been interesting articles on topics unrelated to the …